Transforming Lives Through Genetic Discovery
Over two decades ago when we first opened our doors, we focused on giving much-needed attention to the underserved communities of those with rare diseases. These rare disease communities mostly affected children and were often ignored. At the time, 十大赌博平台排行榜 developed the only treatments for these life-altering conditions, giving hope to patients and families.
Throughout our history, we’ve worked tirelessly to make a difference by pursuing bold science while respecting, educating, and connecting with patients. Through our expertise in genetics and molecular biology, we have been able to develop targeted therapies that address the root cause of the exact conditions we seek to treat.
Our discoveries have led us to countless breakthroughs, best-in-class treatments and many ‘firsts’ in the category. We are grateful to able to better the lives of those struggling with genetic diseases.
As we look forward, we strive to make an even greater impact by applying the same science-driven, patient-forward approach to a broader range of genetic disorders.
The more innovative solutions we develop, the more lives we can impact.
This isn’t just our passion, it’s our purpose.
More than twenty years of transforming lives through genetic discovery.Learn More about our history ⌃
Our management team represents a dynamic cross section of business, clinical and biotechnical expertise.Learn More about our leadership team ⌃
Diversity, Equity & Inclusion
We value diverse perspectives from a broad spectrum of backgrounds, education, personalities, skill sets, experiences, and knowledge.Learn More about Diversity, Equity & Inclusion at 十大赌博平台排行榜 ⌃